Angiodema: Gene therapy treats painful hereditary disorder


In the trial, published in the New England Journal of Medicine, angiodema symptoms were reduced by 95% among a small group of patients from the UK, New Zealand, and the Netherlands given a single infusion – targeted at cells in the liver – to reduce the KLKB1 gene’s ability to produce plasma prekallikrein.



Source link : https://www.bbc.co.uk/news/health-68164372

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Publish date : 2024-02-01 09:55:07

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